More than two years after the Government committed to adding SMA to newborn testing, families are still waiting ...
"Monumental" is how Ashley E. Webb, MD Assistant Professor, Department of Pediatrics, Division of Child & Adolescent Neurology Neuromuscular Program Director, UTHealth, University of Texas Health ...
A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...
A couple whose son died from a rare genetic condition are encouraging others to take part in screening which they say could ...
Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...
"Managing pain in patients with SMA begins with the recognition that there are predictable etiologies leading to pain in SMA and investigating them during each medical visit is important to implement ...
The mother of a four-year-old boy with a rare muscle disease says screening newborn babies for the condition could "save ...
The singer shared an emotional update about her twins’ health on Sunday.
New York, Jan. 26, 2026 (GLOBE NEWSWIRE) -- In recognition of Rare Disease Day on February 28, the Muscular Dystrophy Association (MDA) is sharing powerful community stories throughout the month that ...
Nelson's twin daughters, Ocean Jade and Story Monroe, have been diagnosed with spinal muscular atrophy (SMA) Type 1 ...
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